Year in review 2019: Neuromuscular diseases
| Autor: | David J. Birnkrant, Jane B. Black |
|---|---|
| Rok vydání: | 2020 |
| Předmět: |
musculoskeletal diseases
Pulmonary and Respiratory Medicine medicine.medical_specialty Duchenne muscular dystrophy Cardiomyopathy Spironolactone Eteplirsen Morpholinos Pulmonary function testing chemistry.chemical_compound Humans Medicine Intensive care medicine Oxadiazoles business.industry medicine.disease Eplerenone Ataluren Muscular Dystrophy Duchenne Clinical trial chemistry Pediatrics Perinatology and Child Health Cardiomyopathies business medicine.drug |
| Zdroj: | Pediatric Pulmonology. 55:2542-2546 |
| ISSN: | 1099-0496 8755-6863 |
| Popis: | Neuromuscular cardiopulmonary medicine is entering a new and exciting phase, with studies that assess the respiratory effect of emerging genetic and molecular therapies. In this year's neuromuscular Year in Review, we focus on Duchenne muscular dystrophy (DMD), reviewing studies that evaluate the respiratory effect of eteplirsen, the cardiopulmonary effects of ataluren, and a study comparing the use of spironolactone with eplerenone for the treatment of DMD-related cardiomyopathy. |
| Databáze: | OpenAIRE |
| Externí odkaz: |
|
Plný text