PCR148 Patient Involvement in the Development of Outcomes Measures Specific to Neuronopathic Gaucher Disease Type 2 and Type 3 to Assess HRQoL Over the Disease Journey
Autor: | K Beusterien, J Isaacs, D Jaffe, D Elstein, M Stoodley, E Haf Davies, T Collin-Histed |
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Rok vydání: | 2022 |
Předmět: | |
Zdroj: | Value in Health. 25:S419 |
ISSN: | 1098-3015 |
Databáze: | OpenAIRE |
Externí odkaz: |