High-resolution cellular and molecular follow up of lysosomal disease patients treated with hematopoietic stem cell lentiviral gene therapy

Autor:	Mariana Loperfido, Cristina Baricordi, Aimin Yan, Luigi Barbarossa, Quoc Nguyen, Ingrid Abrahamsen, Stephanie Cherqui, Diana Escolar, Chris Mason, Luca Biasco
Rok vydání:	2022
Předmět:	Endocrinology Endocrinology Diabetes and Metabolism Genetics Molecular Biology Biochemistry
Zdroj:	Molecular Genetics and Metabolism. 135:S75-S76
ISSN:	1096-7192
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::f310dc414d974e1b42bf2315a261df5b https://doi.org/10.1016/j.ymgme.2021.11.193 Zobrazit plný text záznamu Full Text from ScienceDirect