Changes in hematologic and visceral manifestations over time following imiglucerase initiation in Gaucher disease type 1 and type 3 pediatric patients in the ICGG Gaucher Registry

Autor: Pramod K. Mistry, Pablo Bianculli, Isabela Batsu, Walter Heine, Antonio Oliveira-dos-Santos, Pascal Minini, Julie Batista
Rok vydání: 2023
Předmět:
Zdroj: Molecular Genetics and Metabolism. 138:107225
ISSN: 1096-7192
DOI: 10.1016/j.ymgme.2022.107225
Databáze: OpenAIRE