Changes in hematologic and visceral manifestations over time following imiglucerase initiation in Gaucher disease type 1 and type 3 pediatric patients in the ICGG Gaucher Registry
Autor: | Pramod K. Mistry, Pablo Bianculli, Isabela Batsu, Walter Heine, Antonio Oliveira-dos-Santos, Pascal Minini, Julie Batista |
---|---|
Rok vydání: | 2023 |
Předmět: | |
Zdroj: | Molecular Genetics and Metabolism. 138:107225 |
ISSN: | 1096-7192 |
DOI: | 10.1016/j.ymgme.2022.107225 |
Databáze: | OpenAIRE |
Externí odkaz: |