P.105 Safety and effectiveness of onasemnogene abeparvovec (OA) alone or with other disease-modifying therapies (DMTs): Findings from RESTORE

Autor:	L. Servais, K. Benguerba, D. De Vivo, J. Kirschner, F. Muntoni, C. Proud, E. Tizzano, K. Saito, D. Raju, N. LaMarca, R. Sun, F. Anderson, E. Faulkner, R. Finkel
Rok vydání:	2022
Předmět:	Neurology Pediatrics Perinatology and Child Health Neurology (clinical) Genetics (clinical)
Zdroj:	Neuromuscular Disorders. 32:S87
ISSN:	0960-8966
DOI:	10.1016/j.nmd.2022.07.190
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::eacaba48dc97fcf5c6d7a956b8aa424b https://doi.org/10.1016/j.nmd.2022.07.190 Zobrazit plný text záznamu Full Text from ScienceDirect