SA73 Addressing Unmet Needs of Patients With Neuronopathic Gaucher Disease Type 2 and Type 3: Creation of the GARDIAN Patient Registry
| Autor: | T Collin-Histed, J Milce, S Reed, L Braham-Chaouche, D Jaffe, S Revel-Vilk, M Istaiti, M Stoodley, E Haf Davies |
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| Rok vydání: | 2022 |
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| Zdroj: | Value in Health. 25:S497 |
| ISSN: | 1098-3015 |
| DOI: | 10.1016/j.jval.2022.09.2466 |
| Databáze: | OpenAIRE |
| Externí odkaz: |
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