Functional correction of mucopolysaccharidosis I in adult mice by a systemic rAAV9-IDUA gene delivery

Autor:	Douglas M. McCarty, Haiyan Fu, Kathryn Waligura, Marybeth Camboni, Darren Murrey, Aaron S. Meadows
Rok vydání:	2016
Předmět:	Endocrinology business.industry Endocrinology Diabetes and Metabolism Immunology Mucopolysaccharidosis I Genetics Medicine Gene delivery business Molecular Biology Biochemistry
Zdroj:	Molecular Genetics and Metabolism. 117:S79
ISSN:	1096-7192
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::e1d260ab85eb7a2d4bc85199a393f8e6 https://doi.org/10.1016/j.ymgme.2015.12.356 Zobrazit plný text záznamu Full Text from ScienceDirect