1261 Enzyme Replacement Therapy with Velaglucerase Alfa Improves Key Clinical Parameters in a Pediatric Subgroup with Type 1 Gaucher Disease
Autor: | D E Gonzalez, Kiran Bhirangi, Ari Zimran, Deborah Elstein, Eric Crombez |
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Rok vydání: | 2010 |
Předmět: |
Oncology
congenital hereditary and neonatal diseases and abnormalities medicine.medical_specialty business.industry Velaglucerase alfa virus diseases nutritional and metabolic diseases Type 1 Gaucher Disease Enzyme replacement therapy Surgery Internal medicine Pediatrics Perinatology and Child Health Medicine business medicine.drug |
Zdroj: | Pediatric Research. 68:625-625 |
ISSN: | 1530-0447 0031-3998 |
DOI: | 10.1203/00006450-201011001-01261 |
Popis: | 1261 Enzyme Replacement Therapy with Velaglucerase Alfa Improves Key Clinical Parameters in a Pediatric Subgroup with Type 1 Gaucher Disease |
Databáze: | OpenAIRE |
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