P.193 Phosphoryl guanidine-containing backbone modifications enhance exon skipping, dystrophin restoration and survival in a severe mouse model for DMD

Autor:	X. Hu, P. Kandasamy, G. McClorey, M. Shimizu, N. Kothari, N. Iwamoto, M. Byrne, F. Liu, K. Longo, J. Oieni, C. Shivalila, C. Rinaldi, H. Yang, M. Wood, C. Vargeese
Rok vydání:	2022
Předmět:	Neurology Pediatrics Perinatology and Child Health Neurology (clinical) Genetics (clinical)
Zdroj:	Neuromuscular Disorders. 32:S126
ISSN:	0960-8966
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::c7242da84da8df7f39e16e94d76341fe https://doi.org/10.1016/j.nmd.2022.07.348 Zobrazit plný text záznamu Full Text from ScienceDirect