ASPIRO Gene Therapy Trial in X-Linked Myotubular Myopathy (XLMTM): Update on Preliminary Efficacy and Safety Findings

Autor:	A. M. Seferian, Laurent Servais, A. Foley, Suyash Prasad, Salvador Rico, D. N. Saade, Astrid Blaschek, Perry B. Shieh, Wolfgang Müller-Felber, James J. Dowling, M. Noursalehi, Nancy L. Kuntz, Michael W. Lawlor, Carsten G. Bönnemann, W. Miller
Rok vydání:	2021
Předmět:	business.industry Genetic enhancement Medicine business medicine.disease Bioinformatics X-linked myotubular myopathy
Zdroj:	Abstracts of the 46th Annual Meeting of the Society for Neuropediatrics.
ISSN:	1439-1899
DOI:	10.1055/s-0041-1739645
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::bd44a8a086bf20b02662687ef2cbef49 https://doi.org/10.1055/s-0041-1739645 Zobrazit plný text záznamu