4CPS-031 Efficacy and safety of high-dose twice-weekly sebelipase alfa in severe-onset Wolman disease: a case report

Autor: A Castro Balado, MJ de Castro López, P Sánchez Pintos, EJ Bandín Vilar, JM Giráldez Montero, L García Quintanilla, ML Couce Pico, I Zarra Ferro
Rok vydání: 2022
Zdroj: Section 4: Clinical pharmacy services.
DOI: 10.1136/ejhpharm-2022-eahp.78
Databáze: OpenAIRE