PEGTIBATINASE, AN INVESTIGATIONAL ENZYME REPLACEMENT THERAPY FOR THE TREATMENT OF CLASSICAL HOMOCYSTINURIA: INITIAL RESULTS FROM THE PHASE 1/2 COMPOSE STUDY

Autor:	Harvey L. Levy, Janet Thomas, Can Ficicioglu, Melissa Lah, Jaya Ganesh, Marcia Sellos-Moura, Erez M. Bublil, Elizabeth Wilkening, Jalé Güner, Ying Chen, Feriandas Greblikas, Sagar A. Vaidya
Rok vydání:	2022
Předmět:	Endocrinology Endocrinology Diabetes and Metabolism Genetics Molecular Biology Biochemistry
Zdroj:	Molecular Genetics and Metabolism. 135:283-284
ISSN:	1096-7192
DOI:	10.1016/j.ymgme.2022.01.060
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::b2a1bd8b1a914c0b998887299dbbc27a https://doi.org/10.1016/j.ymgme.2022.01.060 Zobrazit plný text záznamu Full Text from ScienceDirect