SBC-102, a recombinant enzyme replacement therapy corrects clinically relevant phenotypic abnormalities in a rat model of lysosomal acid lipase deficiency
Autor: | Wei Hu, Anthony G. Quinn, Alex J. Harvey, Tamas Nagy, Emelie Balmes, Mark C. Leavitt, Angela Lents, Sara Mathews, Michael Chen |
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Rok vydání: | 2011 |
Předmět: | |
Zdroj: | Molecular Genetics and Metabolism. 102:S37 |
ISSN: | 1096-7192 |
DOI: | 10.1016/j.ymgme.2010.11.125 |
Databáze: | OpenAIRE |
Externí odkaz: |