615 Antisense oligonucleotide-based drug development for people with cystic fibrosis carrying the 2789+5 G-to-A splicing mutation

Autor:	Y. Oren, O. Avizur Barchad, E. Ozeri Galai, R. Elgrabli, T. Mordechai, T. Blinder, N. Stanleigh, E. Kerem, B. Kerem
Rok vydání:	2022
Předmět:	Pulmonary and Respiratory Medicine Pediatrics Perinatology and Child Health
Zdroj:	Journal of Cystic Fibrosis. 21:S340-S341
ISSN:	1569-1993
DOI:	10.1016/s1569-1993(22)01305-4
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::86c95098633bc88d7d10a0b5e6f5edff https://doi.org/10.1016/s1569-1993(22)01305-4 Full Text from ScienceDirect