P.103 Onasemnogene abeparvovec (OA) treatment outcomes by patient weight at infusion: Initial findings from the RESTORE registry

Autor:	L. Servais, K. Benguerba, D. De Vivo, J. Kirschner, E. Mercuri, F. Muntoni, C. Proud, E. Tizzano, S. Quijano-Roy, K. Saito, D. Raju, N. LaMarca, R. Sun, F. Anderson, E. Faulkner, R. Finkel
Rok vydání:	2022
Předmět:	Neurology Pediatrics Perinatology and Child Health Neurology (clinical) Genetics (clinical)
Zdroj:	Neuromuscular Disorders. 32:S87
ISSN:	0960-8966
DOI:	10.1016/j.nmd.2022.07.188
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::84cb3d14b53c42cd66564b886532dffb https://doi.org/10.1016/j.nmd.2022.07.188 Zobrazit plný text záznamu Full Text from ScienceDirect