P.53 Muscle microRNAs in the cerebrospinal fluid predict clinical response to nusinersen therapy in type II and type III spinal muscular atrophy patients

Autor:	I. Magen, S. Aharoni, N. Yacovzada, I. Tokatly Latzer, C. Alves, L. Sagi, A. Fattal-Valevski, K. Swoboda, J. Katz, E. Bruckheimer, Y. Nevo, E. Hornstein
Rok vydání:	2022
Předmět:	Neurology Pediatrics Perinatology and Child Health Neurology (clinical) Genetics (clinical)
Zdroj:	Neuromuscular Disorders. 32:S62
ISSN:	0960-8966
DOI:	10.1016/j.nmd.2022.07.089
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::71396c4624e5a63dcaa8b595a271fcbd https://doi.org/10.1016/j.nmd.2022.07.089 Zobrazit plný text záznamu Full Text from ScienceDirect