Relevance and comprehension of patient-reported outcome measures of mobility, physical function, and speech among patients with late-onset GM2 gangliosidoses
Autor: | Alaa Hamed, Ruth Pulikottil-Jacob, Chad Gwaltney, Nicholas Stephens, Nicole Lyn, Camille Rochmann, Robert Krupnick |
---|---|
Rok vydání: | 2020 |
Předmět: |
medicine.medical_specialty
GM2 gangliosidoses business.industry Endocrinology Diabetes and Metabolism Late onset Audiology Physical function medicine.disease Biochemistry Comprehension Endocrinology Genetics Medicine Relevance (information retrieval) Patient-reported outcome business Molecular Biology |
Zdroj: | Molecular Genetics and Metabolism. 129:S133 |
ISSN: | 1096-7192 |
Databáze: | OpenAIRE |
Externí odkaz: |