Immunogenicity of cipaglucosidase alfa/miglustat versus alglucosidase alfa/placebo in late-onset Pompe disease (LOPD): A phase III, randomized study (PROPEL)

Autor:	Yin-Hsiu Chien, Elfrida Benjamin, Benedikt Schoser, Priya Kishnani, Tahseen Mozaffar, Jordi Díaz-Manera, Franklin Johnson, Sheela Sitaraman Das, Anju Nair, Hadis Williams, Eric Anderson, John T. Mondick, Anthony Sileno
Rok vydání:	2022
Předmět:	Endocrinology Endocrinology Diabetes and Metabolism Genetics Molecular Biology Biochemistry
Zdroj:	Molecular Genetics and Metabolism. 135:S30
ISSN:	1096-7192
DOI:	10.1016/j.ymgme.2021.11.062
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=doi_________::6b5ab9215e6b20c7e51c48a2743ba63f https://doi.org/10.1016/j.ymgme.2021.11.062 Zobrazit plný text záznamu Full Text from ScienceDirect