Safety and clinical outcomes in children with acid sphingomyelinase deficiency were not impacted by a change in the olipudase alfa drug manufacturing process: ASCEND-Peds 1-year subanalysis
| Autor: | Monica Kumar, Nicole Armstrong, Yong Kim, Jing Li, Susan Richards, Abhimanyu Yarramaneni, Qi Zhang, Mario Aguiar |
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| Rok vydání: | 2023 |
| Předmět: | |
| Zdroj: | Molecular Genetics and Metabolism. 138:107188 |
| ISSN: | 1096-7192 |
| DOI: | 10.1016/j.ymgme.2022.107188 |
| Databáze: | OpenAIRE |
| Externí odkaz: |
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