PCR70 Avalglucosidase Alfa (AVA) Improves Symptoms and Functioning in Late-Onset Pompe Disease (LOPD) Patients vs Alglucosidase Alfa (ALG): Post-Hoc Analyses of Patient-Reported Outcomes (PROs) From COMET Trial

Autor: A Toscano, AT van der Ploeg, KI Berger, MM Dimachkie, B Schoser, C Gwaltney, J Msihid, A Hamed, N Thibault, L Pollissard, PS Kishnani
Rok vydání: 2022
Předmět:
Zdroj: Value in Health. 25:S403
ISSN: 1098-3015
DOI: 10.1016/j.jval.2022.09.2005
Databáze: OpenAIRE