Are we prepared to deliver gene‐targeted therapies for rare diseases?
| Autor: | Timothy W. Yu, Stephen F. Kingsmore, Robert C. Green, Tippi MacKenzie, Melissa Wasserstein, Michele Caggana, Nina B. Gold, Annie Kennedy, Priya S. Kishnani, Matthew Might, Phillip J. Brooks, Jill A. Morris, Melissa A. Parisi, Tiina K. Urv |
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| Rok vydání: | 2023 |
| Předmět: | |
| Zdroj: | American Journal of Medical Genetics Part C: Seminars in Medical Genetics. 193:7-12 |
| ISSN: | 1552-4876 1552-4868 |
| DOI: | 10.1002/ajmg.c.32029 |
| Databáze: | OpenAIRE |
| Externí odkaz: |
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