P040 Compassionate use triple therapy CFTR modulation (Kaftrio®) in severe disease. Single-centre, real-world clinical outcomes, safety and tolerability
Autor: | M. McCarthy, C. Howlett, D. Morrissy, S. Twohig, Desmond M. Murphy, Barry J. Plant, Tamara Vagg, C. Fleming, Yvonne McCarthy, J. Dorgan |
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Rok vydání: | 2021 |
Předmět: | |
Zdroj: | Journal of Cystic Fibrosis. 20:S50-S51 |
ISSN: | 1569-1993 |
DOI: | 10.1016/s1569-1993(21)01067-5 |
Popis: | Objective: Patients (F508del/F508del or F508del/MF) with severe CF (ppFEV1 |
Databáze: | OpenAIRE |
Externí odkaz: |