P040 Compassionate use triple therapy CFTR modulation (Kaftrio®) in severe disease. Single-centre, real-world clinical outcomes, safety and tolerability

Autor: M. McCarthy, C. Howlett, D. Morrissy, S. Twohig, Desmond M. Murphy, Barry J. Plant, Tamara Vagg, C. Fleming, Yvonne McCarthy, J. Dorgan
Rok vydání: 2021
Předmět:
Zdroj: Journal of Cystic Fibrosis. 20:S50-S51
ISSN: 1569-1993
DOI: 10.1016/s1569-1993(21)01067-5
Popis: Objective: Patients (F508del/F508del or F508del/MF) with severe CF (ppFEV1
Databáze: OpenAIRE