Local restoration of dystrophin expression with the morpholino oligomer AVI-4658 in Duchenne muscular dystrophy: a single-blind, placebo-controlled, dose-esclation, proof-of-concept study
Autor: | Kinali, M, Arechavala-Gomeza, V, Feng, L, Cirak, S, Hunt, D, Adkin, C, Guglieri, M, Ashton, E, Abbs, S, Nihoyannopoulos, P, Garralda, M E, Rutherford, M, McCulley, C, Popplewell, L, Graham, I R, Dickson, G, Wood, M J, Wells, D J, Wilton, S D, Kole, R, Staub, V, Bushby, K, Sewry, C, Morgan, J E, Muntoni, F, Guy's Hospital, London, Hammersmith Hospital, Imperial College London, Institute of Child Health, London, Newcastle, St Mary's Hospital, London |
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Jazyk: | angličtina |
Rok vydání: | 2009 |
Zdroj: | Lancet Neurology |
Databáze: | OpenAIRE |
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