The TREAT-NMD advisory committee for therapeutics (TACT): an innovative de-risking model to foster orphan drug development

Autor:	Heslop, E, Csimma, C, Straub, V, McCall, J, Nagaraju, K, Wagner, K R, Caizergues, D, Korinthenberg, R, Flanigan, K M, Kaufmann, P, McNeil, E, Mendell, J, Hesterlee, S, Wells, D J
Jazyk:	angličtina
Zdroj:	ORPHANET JOURNAL OF RARE DISEASES
Databáze:	OpenAIRE
Externí odkaz:	https://explore.openaire.eu/search/publication?articleId=core_ac_uk__::9b31e2daa2c458ab73fc85a877baeddb https://researchonline.rvc.ac.uk/id/eprint/9251/1/9251.pdf Zobrazit plný text záznamu