Replacing the Enzyme α-L-Iduronidase at Birth Ameliorates Symptoms in the Brain and Periphery of Dogs with Mucopolysaccharidosis Type I.

Autor: Dierenfeld, Ashley D., McEntee, Michael F., Vogler, Carole A., Vite, Charles H., Chen, Agnes H., Passage, Merry, Le, Steven, Shah, Sahil, Jens, Jackie K., Snella, Elizabeth M., Kline, Karen L., Parkes, Jennifer D., Ware, Wendy A., Moran, Lori E., Fales-Williams, Amanda J., Wengert, Jane A., Whitley, R. David, Betts, Daniel M., Boal, Amy M., Riedesel, Elizabeth A.
Zdroj: Science Translational Medicine; 12/1/2010, Vol. 2 Issue 60, preceding p1-8, 9p
Databáze: Complementary Index