Real-World Data in Children with Spinal Muscular Atrophy Type 1 on Long-Term Ventilation Receiving Gene Therapy: A Prospective Cohort Study.

Autor: Alajjuri, Mohammad Ala', Abusamra, Rania, Mundada, Vivek, Narayan, Omendra
Zdroj: Advances in Respiratory Medicine (MDPI); Oct2024, Vol. 92 Issue 5, p338-347, 10p
Databáze: Complementary Index