Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease.

Autor: Massaro, Giulia, Geard, Amy F, Nelvagal, Hemanth R, Gore, Katrina, Clemo, Nadine K, Waddington, Simon N, Rahim, Ahad A
Zdroj: Human Molecular Genetics; 9/1/2024, Vol. 33 Issue 17, p1467-1480, 14p
Databáze: Complementary Index