Regulatory news: Olipudase alfa‐rpcp (Xenpozyme™) for treatment of non‐central nervous system manifestations of acid sphingomyelinase deficiency (ASMD) in adult and pediatric patients—FDA Approval summary.
| Autor: | Hon, Yuen Yi, Zaidi, Anita, Giffin, Andrew, Wang, Yan, Lei, Nie, Hossain, Md Nayeem, Wang, Jie, Li, Hongshan, Liu, Guansheng, Liu, Jiang, Yang, Yuching, Zhu, Hao, Pacanowski, Michael, McLeod‐Flynn, Laurie, Summan, Mukesh, Liu, Yongmin, Sheikh, Faruk, Dickensheets, Harold, Kim, Jennifer, McWilliams, Ian |
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| Zdroj: | Journal of Inherited Metabolic Disease; Jul2024, Vol. 47 Issue 4, p575-577, 3p |
| Databáze: | Complementary Index |
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