Management of Select Adverse Events Following Delandistrogene Moxeparvovec Gene Therapy for Patients With Duchenne Muscular Dystrophy.
Autor: | Zaidman, Craig M., Goedeker, Natalie L., Aqul, Amal A., Butterfield, Russell J., Connolly, Anne M., Crystal, Ronald G., Godwin, Kara E., Hor, Kan N., Mathews, Katherine D., Proud, Crystal M., Kula Smyth, Elizabeth, Veerapandiyan, Aravindhan, Watkins, Paul B., Mendell, Jerry R. |
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Zdroj: | Journal of Neuromuscular Diseases; 2024, Vol. 11 Issue 3, p687-699, 13p |
Databáze: | Complementary Index |
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