Increase in Full-Length Dystrophin by Exon Skipping in Duchenne Muscular Dystrophy Patients with Single Exon Duplications: An Open-label Study.
| Autor: | Nicolau, Stefan, Malhotra, Jyoti, Kaler, Maryann, Magistrado-Coxen, Pamela, Iammarino, Megan A., Reash, Natalie F., Frair, Emma C., Wijeratne, Saranga, Kelly, Benjamin J., White, Peter, Lowes, Linda P., Waldrop, Megan A., Flanigan, Kevin M. |
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| Zdroj: | Journal of Neuromuscular Diseases; 2024, Vol. 11 Issue 3, p679-685, 7p |
| Databáze: | Complementary Index |
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