P1548: LONG‐TERM TREATMENT WITH ORAL MITAPIVAT IS ASSOCIATED WITH NORMALIZATION OF HEMOGLOBIN LEVELS IN PATIENTS WITH PYRUVATE KINASE DEFICIENCY.

Autor: Barcellini, W., Grace, R. F., Al‐Samkari, H., Glenthøj, A., Rothman, J. A., Morado Arias, M., Layton, D. M., Andres, O., DiBacco, M., Hawkins, P., Judge, M. P., Tai, F., Morales‐Arias, J., Beynon, V., van Beers, E. J.
Zdroj: HemaSphere; 2022 Supplement 3, Vol. 6, p1429-1430, 2p
Databáze: Complementary Index