Utilizing AAV-mediated LEAPER 2.0 for programmable RNA editing in non-human primates and nonsense mutation correction in humanized Hurler syndrome mice.

Autor: Yi, Zongyi, Zhao, Yanxia, Yi, Zexuan, Zhang, Yongjian, Tang, Gangbin, Zhang, Xiaoxue, Tang, Huixian, Zhang, Wei, Zhao, Ying, Xu, Huayuan, Nie, Yuyang, Sun, Xueqing, Xing, Lijun, Dai, Lian, Yuan, Pengfei, Wei, Wensheng
Zdroj: Genome Biology; 10/23/2023, Vol. 24 Issue 1, p1-20, 20p
Databáze: Complementary Index