Current avenues of gene therapy in Pompe disease.

Autor: Leon-Astudillo, Carmen, Trivedi, Prasad D., Sun, Ramon C., Gentry, Matthew S., Fuller, David D., Byrne, Barry J., Corti, Manuela
Zdroj: Current Opinion in Neurology; Oct2023, Vol. 36 Issue 5, p464-473, 10p
Databáze: Complementary Index