AAV9-mediated SMN gene therapy rescues cardiac desmin but not lamin A/C and elastin dysregulation in Smn2B/− spinal muscular atrophy mice.
Autor: | Brown, Sharon J, Šoltić, Darija, Synowsky, Silvia A, Shirran, Sally L, Chilcott, Ellie, Shorrock, Hannah K, Gillingwater, Thomas H, Yáñez-Muñoz, Rafael J, Schneider, Bernard, Bowerman, Melissa, Fuller, Heidi R |
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Zdroj: | Human Molecular Genetics; 10/15/2023, Vol. 32 Issue 20, p2950-2965, 16p |
Databáze: | Complementary Index |
Externí odkaz: |