Use of Elamipretide in patients assigned treatment in the compassionate use program: Case series in pediatric patients with rare orphan diseases.

Autor: Koenig, Mary Kay, Russo, Sam Nick, McBride, Kim L., Bjornsson, Hans Tomas, Gunnarsdottir, Brynja Bjork, Goldstein, Amy, Falk, Scott A.
Zdroj: Journal of Inherited Metabolic Disease Reports; Jan2023, Vol. 64 Issue 1, p65-70, 6p
Databáze: Complementary Index
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