Gene therapy for Crigler Najjar syndrome: results of the dose finding part of the CareCN, phase 1-2 clinical trial.

Autor: D'Antiga, L., Beuers, U., Brunetti-Pierri, N., Baumann, U., Di Giorgio, A., Aronson, S., Hubert, A., Romano, R., Junge, N., Bosma, P., Bortolussi, G., Muro, A. F., Pavlyuk, M., Veron, P., Ronzitti, G., Collaud, F., Knuchel-Legendre, N., Mingozzi, F., Labrune, P.
Zdroj: Journal of Pediatric Gastroenterology & Nutrition; 2022 Supplement, Vol. 74, p674-675, 2p
Databáze: Complementary Index
Externí odkaz: