Identification and Optimization of a Minor Allele-Specific siRNA to Prevent PNPLA3 I148M-Driven Nonalcoholic Fatty Liver Disease.

Autor: Murray, Justin K., Long, Jason, Liu, Lei, Singh, Shivani, Pruitt, Danielle, Ollmann, Michael, Swearingen, Elissa, Hardy, Miki, Homann, Oliver, Wu, Bin, Holder, Jerry Ryan, Sham, Kelvin, Herberich, Brad, Lo, Mei-Chu, Dou, Hui, Shkumatov, Artem, Florio, Monica, Rulifson, Ingrid C.
Zdroj: Nucleic Acid Therapeutics; Oct2021, Vol. 31 Issue 5, p324-340, 17p
Databáze: Complementary Index