Systemic Evaluation of Chimeric LNA/2′-O-Methyl Steric Blockers for Myotonic Dystrophy Type 1 Therapy.

Autor: Christou, Melina, Wengel, Jesper, Sokratous, Kleitos, Kyriacou, Kyriacos, Nikolaou, Georgios, Phylactou, Leonidas A., Mastroyiannopoulos, Nikolaos P.
Zdroj: Nucleic Acid Therapeutics; Apr2020, Vol. 30 Issue 2, p80-93, 14p
Databáze: Complementary Index