Onasemnogene Abeparvovec Gene-Replacement Therapy (GRT) in Pre-symptomatic Spinal Muscular Atrophy (SMA): SPR1NT Study Update.
| Autor: | Schultz, Meredith, Swoboda, Kathryn J., Farrar, Michelle, McMillan, Hugh, Parsons, Julie, Ernst, Uwe, Kernbauer, Elaine, Farrow, Marcia, Ogrinc, Francis G., Kavanagh, Sarah, Feltner, Douglas E., McGill, Bryan E., Spector, Sidney A., L'Italien, James, Sproule, Douglas, Strauss, Kevin |
|---|---|
| Předmět: | |
| Zdroj: | Neuropediatrics; 2019 Supplement2, Vol. 50, pS1-S55, 55p |
| Databáze: | Complementary Index |
| Externí odkaz: |
|