Novel Vector Design and Hexosaminidase Variant Enabling Self-Complementary Adeno-Associated Virus for the Treatment of Tay-Sachs Disease.

Autor: Karumuthil-Melethil, Subha, Kalburgi, Sahana Nagabhushan, Thompson, Patrick, Tropak, Michael, Kaytor, Michael D., Keimel, John G., Mark, Brian L., Mahuran, Don, Walia, Jagdeep S., Gray, Steven J.
Zdroj: Human Gene Therapy; Jul2016, Vol. 27 Issue 7, p509-521, 13p
Databáze: Complementary Index