Second gene therapy for hemophilia B approved: More answers or questions?

Autor: Kaczmarek R; Department of Pediatrics, Indiana University School of Medicine, Indianapolis, IN, USA. Electronic address: rkaczmar@iu.edu., Pierce GF; World Federation of Hemophilia, Montreal, QC, Canada. Electronic address: gpierce@wfh.org.
Jazyk: angličtina
Zdroj: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2024 Nov 29. Date of Electronic Publication: 2024 Nov 29.
DOI: 10.1016/j.ymthe.2024.11.026
Databáze: MEDLINE