Weighing the Risks of Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy.

Autor: Dunbar CE; From the Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, Maryland.
Jazyk: angličtina
Zdroj: The New England journal of medicine [N Engl J Med] 2024 Oct 10; Vol. 391 (14), pp. 1358-1359.
DOI: 10.1056/NEJMe2409399
Databáze: MEDLINE