Compassionate use trials and equitable access to variant-specific treatment for cystic fibrosis.

Autor: Odem-Davis K; Seattle Children's Research Institute, Seattle, WA 98145-5005, USA. Electronic address: katherine.davis@seattlechildrens.org., Taylor-Cousar JL; Departments of Internal Medicine and Pediatrics, National Jewish Health, Denver, CO, USA.
Jazyk: angličtina
Zdroj: The Lancet. Respiratory medicine [Lancet Respir Med] 2024 Aug 13. Date of Electronic Publication: 2024 Aug 13.
DOI: 10.1016/S2213-2600(24)00243-1
Abstrakt: Competing Interests: KO-D is an employee at the Cystic Fibrosis Therapeutics Development Network (CF TDN) Coordinating Center at Seattle Children's Research Institute, with salary indirectly supported through the Cystic Fibrosis Foundation (CFF). JLT-C reports, as a faculty at an institution that is part of the CF TDN, site or national principal investigator roles on studies for 4DMT, Vertex, and Eloxx; grant funding from the CFF and NIH; payments to the institution for clinical trial advisory efforts from Vertex and 4DMT; travel support to participate in CFF Board of Trustees meetings from the CFF; past payments as Chair of an AbbVie data monitoring committee; role as adult patient care representative to the CFF Board of Trustees; serving on the CFF's Clinical Research Executive Committee, CFF advisory board, Racial Justice Working Group, scientific advisory board for Emily's Entourage, ATS Scientific Grant Review Committee, the Respiratory Research Awards Committee, and the NHLBI Clinical Trials Study Section; oles as immediate past Chair of the CF TDN's Sexual Health, Reproduction and Gender Research-Working Group, and Co-Chair of the Heath Equity Team Science Awards study section; role as current Chair-Elect for the ATS International Conference Committee; and membership of the International Advisory Board of The Lancet Respiratory Medicine and the Editorial Board of the Journal of Cystic Fibrosis.
Databáze: MEDLINE