Landmark endorsement of a global registry: The European Medicines Agency (EMA) Committee for Medicinal Products for Human Use (CHMP), publicly endorses World Federation of Hemophilia Gene Therapy Registry as global standard.

Autor: Konkle BA; Washington Center for Bleeding Disorders, University of Washington, Seattle, Washington, USA., Peyvandi F; International Society on Thrombosis and Hemostasis, Carrboro, North Carolina, USA., Coffin D; World Federation of Hemophilia, Montreal, Quebec, Canada., Naccache M; World Federation of Hemophilia, Montreal, Quebec, Canada., Youttananukorn T; World Federation of Hemophilia, Montreal, Quebec, Canada., Pierce GF; World Federation of Hemophilia, Montreal, Quebec, Canada.
Jazyk: angličtina
Zdroj: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2024 Jan; Vol. 30 (1), pp. 232-235. Date of Electronic Publication: 2023 Dec 18.
DOI: 10.1111/hae.14912
Databáze: MEDLINE
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