Corrigendum to "The long-term safety and efficacy of vestronidase alfa, rhGUS enzyme replacement therapy, in subjects with mucopolysaccharidosis VII" [Mol Genet Metab 2020 Mar;129(3):219-227].

Autor: Wang RY; Division of Metabolic Disorders, Children's Hospital of Orange County, 1201 W. La Veta Ave, Orange, CA 92868, United States; Department of Pediatrics, University of California-Irvine, Orange, CA 92868, United States. Electronic address: RaWang@choc.org., da Silva Franco JF; Hospital Sabara, Av. Angélica, 1987 Consolação, São Paulo, SP 01227-200, Brazil; Centro de Biotecnologia, Instituto de Pesquisas de Energéticas e Nucleares IPEN/USP, Av 11 de junho 364, Casa 3, Vila Clementino, São Paulo 04041-001, Brazil., López-Valdez J; Centenario Hospital Miguel Hidalgo, Av. Gomez Morin S/N, La estación- La Alameda, Aguascalientes Ags 20259, Mexico., Martins E; Centro Hospitalar Do Porto, Hospital de Santo António, Porto, Largo do Prof. Abel Salazar, 4099-001 Porto, Portugal., Sutton VR; Department of Molecular & Human Genetics Baylor College of Medicine, Texas Children's Hospital, Mail Stop BCM225, Houston, TX 77030, United States. Electronic address: vrsutton@texaschildrens.org., Whitley CB; Department of Pediatrics, and Experimental and Clinical Pharmacology, University of Minnesota, East Building, 2450 Riverside Ave, Minneapolis, MN 55454, United States. Electronic address: whitley@umn.edu., Zhang L; Ultragenyx Pharmaceutical Inc., 60 Leveroni Ct, Novato, CA 94949, United States. Electronic address: LZhang@ultragenyx.com., Cimms T; Ultragenyx Pharmaceutical Inc., 60 Leveroni Ct, Novato, CA 94949, United States. Electronic address: TCimms@ultragenyx.com., Marsden D; Ultragenyx Pharmaceutical Inc., 60 Leveroni Ct, Novato, CA 94949, United States. Electronic address: DMarsden@ultragenyx.com., Jurecka A; Ultragenyx Pharmaceutical Inc., 60 Leveroni Ct, Novato, CA 94949, United States. Electronic address: AJurecka@ultragenyx.com., Harmatz P; UCSF Benioff Children's Hospital Oakland, 744 52nd St, Oakland, CA 94609, United States. Electronic address: Paul.Harmatz@UCSF.edu.
Jazyk: angličtina
Zdroj: Molecular genetics and metabolism [Mol Genet Metab] 2020 Sep - Oct; Vol. 131 (1-2), pp. 285. Date of Electronic Publication: 2020 Aug 23.
DOI: 10.1016/j.ymgme.2020.08.001
Databáze: MEDLINE