Efficacy of hematopoietic cell transplantation in metachromatic leukodystrophy: the Dutch experience.

Autor: van Rappard DF; Department of Pediatric Neurology, Center for Childhood White Matter Disorders, VU University Medical Center, and Neuroscience Campus Amsterdam, Amsterdam, The Netherlands;, Boelens JJ; Department of Pediatrics, Blood and Marrow Transplantation Program, Laboratory of Translational Immunology and Department of Hematology, and Sylvia Toth Center for Multidisciplinary Follow up after Hematopoietic Cell Transplantation, University Medical Center Utrecht, Utrecht, The Netherlands;, van Egmond ME; Department of Pediatric Neurology, Center for Childhood White Matter Disorders, VU University Medical Center, and Neuroscience Campus Amsterdam, Amsterdam, The Netherlands; University of Groningen, Department of Neurology, University Medical Center Groningen, Groningen, The Netherlands; Department of Neurology, Ommelander Ziekenhuis Groningen, Delfzijl and Winschoten, The Netherlands;, Kuball J; Laboratory of Translational Immunology and Department of Hematology, and., van Hasselt PM; Sylvia Toth Center for Multidisciplinary Follow up after Hematopoietic Cell Transplantation, University Medical Center Utrecht, Utrecht, The Netherlands; Department of Pediatric Metabolic Disorders, University Medical Center Utrecht, Utrecht, The Netherlands;, Oostrom KJ; Department of Pediatric Psychology, VU University Medical Center Amsterdam, Amsterdam, The Netherlands;, Pouwels PJ; Department of Physics and Medical Technology, VU University Medical Center, and Neuroscience Campus Amsterdam, Amsterdam, The Netherlands; and., van der Knaap MS; Department of Pediatric Neurology, Center for Childhood White Matter Disorders, VU University Medical Center, and Neuroscience Campus Amsterdam, Amsterdam, The Netherlands;, Hollak CE; Division of Endocrinology and Metabolism, Department of Internal Medicine, Academic Medical Center Amsterdam, Amsterdam, The Netherlands., Wolf NI; Department of Pediatric Neurology, Center for Childhood White Matter Disorders, VU University Medical Center, and Neuroscience Campus Amsterdam, Amsterdam, The Netherlands;
Jazyk: angličtina
Zdroj: Blood [Blood] 2016 Jun 16; Vol. 127 (24), pp. 3098-101. Date of Electronic Publication: 2016 Apr 26.
DOI: 10.1182/blood-2016-03-708479
Databáze: MEDLINE