Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: alpha-, beta-, gamma-, or delta-sarcoglycan gene delivered with intramuscular instillations of adeno-associated vectors.
| Autor: | Stedman H; University of Pennsylvania Health System, Institute for Human Gene Therapy, Philadelphia 19104, USA., Wilson JM, Finke R, Kleckner AL, Mendell J |
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| Jazyk: | angličtina |
| Zdroj: | Human gene therapy [Hum Gene Ther] 2000 Mar 20; Vol. 11 (5), pp. 777-90. |
| DOI: | 10.1089/10430340050015671 |
| Databáze: | MEDLINE |
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