Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open-label trial.
Autor: | Gaudet, D1, Méthot, J1, Déry, S2, Brisson, D1, Essiembre, C2, Tremblay, G2, Tremblay, K1, de Wal, J3, Twisk, J3, van den Bulk, N3, Sier-Ferreira, V3, van Deventer, S3 |
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Zdroj: | Gene Therapy. Apr2013, Vol. 20 Issue 4, p361-369. 9p. |
Databáze: | Academic Search Ultimate |
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