Efficacy of Gene Therapy for a Prototypical Lysosomal Storage Disease (GSD-II) Is Critically Dependent on Vector Dose, Transgene Promoter, and the Tissues Targeted for Vector Transduction
| Autor: | Ding, Enyu1, Hu, Huimin1, Hodges, Bradley L.1, Migone, Felicia1, Serra, Delila1, Xu, Fang1, Chen, Yuan-Tsong1,2, Amalfitano, Andrea1,2 |
|---|---|
| Zdroj: | Molecular Therapy. Apr2002, Vol. 5 Issue 4, p436. 11p. |
| Databáze: | Academic Search Ultimate |
| Externí odkaz: |
|