908. Design and Optimization of U7snRNAs for Skipping of Exon 51 in DMD: Promising Tools for Future Clinical Trials.
Autor: | Goyenvalle, Aurelie1, Vulin, Adeline1, Lorain, Stephanie1, Aartsma-Rus, Annemieke2, van Deutekom, Judith C. T.2, Danos, Olivier1, Garcia, Luis1 |
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Zdroj: | Molecular Therapy. Jun2006, Vol. 13, pS350-S350. 1p. |
Databáze: | Academic Search Ultimate |
Externí odkaz: |