908. Design and Optimization of U7snRNAs for Skipping of Exon 51 in DMD: Promising Tools for Future Clinical Trials.

Autor: Goyenvalle, Aurelie1, Vulin, Adeline1, Lorain, Stephanie1, Aartsma-Rus, Annemieke2, van Deutekom, Judith C. T.2, Danos, Olivier1, Garcia, Luis1
Zdroj: Molecular Therapy. Jun2006, Vol. 13, pS350-S350. 1p.
Databáze: Academic Search Ultimate